While right-wing populism surges in some of the world’s leading democracies, Chile’s leftist government is rushing in the ...

The Ed Morse MDA Golf Tournament is happening May 9 at PGA National. The Ed Morse MDA Golf Tournament is happening May 9 at PGA National.

John Brandsema, MD, a pediatric neurologist at Children’s Hospital of Philadelphia, speaks with Healio about the current understanding of the genetic factors behind muscular dystrophy.

"The work that Muscular Dystrophy Association is doing - funding research ... This year, the organizations are also prioritizing research into the causes of heightened prevalence of ALS among fire ...

Mutation suppression therapy for Duchenne muscular dystrophy is targeted to the particular mutation that causes muscular dystrophy. Additionally, nonsense mutation suppression therapy may be of ...

A major trial of a promising gene therapy for Duchenne muscular dystrophy has fallen short ... condition that primarily affects boys. It causes relentless muscle breakdown, loss of mobility ...

It causes relentless muscle breakdown ... Is dystrophin immunogenicity a barrier to advancing gene therapy for Duchenne muscular dystrophy? Gene Therapy (2025). DOI: 10.1038/s41434-025-00531 ...

This causes the muscles to progressively weaken and lose function ... Duvyzat was designated as an orphan medicinal product on 04 July 2012 treatment of Duchenne muscular dystrophy. Following this ...