Experts make case for early testing, prevention and care In this report, VINCENT KURAUN explores the groundbreaking ...

The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely ...

The baby, KJ Muldoon of Clifton Heights, Penn., is one of 350 million people worldwide with rare diseases, most of which are ...

In a world first, a child diagnosed with a rare metabolic disorder has been successfully treated with a customized CRISPR ...

The technique used on a 9½-month-old boy with a rare condition has the potential to help people with thousands of other ...

Editas Medicine reports successful gene editing levels in stem cells, supporting potential treatment for sickle cell disease and beta thalassemia. Editas Medicine announced promising new data on ...

Health camp certifies 35 sickle cell patients for disability benefits, emphasizing prevention, early detection, and community support.

A CRISPR treatment seems to have been effective for a baby’s devastating disease, but it is not clear whether such bespoke ...

In June, the Centers for Medicare & Medicaid Services (CMS) will name the participating states for the agency’s new Cell and ...

A team of doctors and scientists have successfully treated a rare genetic condition with the first-ever personalized ...

A nine-month-old baby has become the first person ever to be successfully treated with personalized gene editing therapy. Researchers corrected a specific gene mutation in baby KJ Muldoon‘s liver ...