The amino acid glutamine plays an unexpected role in erythropoiesis, the differentiation of erythroid progenitor cells into ...

“We show this process is impaired in various red blood cell disorders, such as β-thalassemia,” Xu said. “This causes a ...

Rocket Pharmaceuticals, Inc. , a fully integrated, late-stage biotechnology company advancing a sustainable pipeline of genetic therapies for rare disorders with high unmet need, today announced that ...

Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT), a fully integrated, late-stage biotechnology company advancing a sustainable pipeline of genetic therapies for rare disorders with high unmet need, today ...

Mirae Asset Global Investments Co. Ltd. raised its position in Rocket Pharmaceuticals, Inc. (NASDAQ:RCKT – Free Report) by 21.5% during the third quarter, according to its most recent filing with the ...

About PYRUKYND® (mitapivat) PYRUKYND is a pyruvate kinase activator indicated for the treatment of hemolytic anemia in adults with pyruvate kinase (PK) deficiency in the United States, and for the ...

Q3 2024 Earnings Call Transcript October 31, 2024 Operator: Good morning, and welcome to Agios’ Third Quarter 2024 Conference Call. [Operator Instructions] Please be advised that today’s call is being ...

We are especially focused on rare diseases that result in the dysfunction and destruction of red blood cells, including pyruvate kinase deficiency or PKD, thalassemia, sickle cell disease and ...

Mitapivat is approved under the name Pyrukynd to treat a genetic disorder called pyruvate kinase deficiency that causes red blood cells to die prematurely. It’s designed to boost energy production in ...