Grey’s Anatomy star Eric Dane is opening up for the first time in an interview after receiving devastating news of an ALS ...

The findings support the clinical benefits of delandistrogene moxeparvovec in patients with Duchenne muscular dystrophy (DMD) ...

PepGen Inc. overstated prospects for its leading product candidate to treat a muscle-degenerating genetic disorder before facing negative responses to its clinical trial data and ultimately stopping ...

Solve FSHD and Modalis Therapeutics Corp. have established a strategic collaboration to develop an innovative therapy for facioscapulohumeral muscular dystrophy (FSHD).

Avidity has been given the go-ahead by the FDA to request accelerated approval of delpacibart braxlosiran—potentially the ...

The campaign to commemorate the work of the Muscular Dystrophy Association was created in partnership with agency Yes&.

As diagnoses of autism spectrum disorder rise, a UNLV researcher's breakthrough could lead to new forms of treatment ...

Hundreds gathered to support muscular dystrophy research as the Muscular Dystrophy Association marked its 75th anniversary.

Repurposing existing therapies may help slow muscle weakness in patients with Duchenne muscular dystrophy, a new study ...

In many genetic diseases, a small error in the DNA code can have devastating effects. These errors, called nonsense mutations ...

Scientists present current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec. AAN Evidence in Focus articles highlight the strength of the current ...

Duchenne muscular dystrophy (DMD) is a rare neurological condition that causes severe muscle weakness and intellectual disability. DMD is an inherited (passed down) disorder. The condition is ...