A man with a rare muscle-wasting condition said he feels "deflated" that a drug that improves his symptoms has not been ...

The drug, Givinostat, has been approved as safe for use but Belfast Health Trust, NI's specialist centre for the condition, ...

Sarepta Therapeutics ( NASDAQ: SRPT) reported a second fatality from acute liver failure in a patient treated with its gene ...

Mr Steven Eng has been helping with daily activities like going to the bathroom and showering. Read more at straitstimes.com.

Couple campaigning for the Government to sanction pay for a new drug called givinostat, which slows down muscle-wasting ...

Hundreds gathered to support muscular dystrophy research as the Muscular Dystrophy Association marked its 75th anniversary.

Burn Boot Camp is proud to announce the success of its ninth annual "Be Their Muscle" fundraising campaign for the Muscular ...

Avidity has been given the go-ahead by the FDA to request accelerated approval of delpacibart braxlosiran—potentially the ...

The parents of a nine-year-old boy battling a devastating muscle-wasting condition say new research could offer them more ...

U.S. FDA successfully completed Pre-License Inspection; Company expects facility will meet all requirements to support ...

Parents of children with an incurable muscle-wasting condition have called on the Minister for Health to accelerate the ...

Over 300 people came out Thursday night for the annual “All That Jazz” Gala benefiting the Muscular Dystrophy Association. Since 2014, nearly $2 million dollars have been raised by MDA, which is the ...