A 46-year-old woman with type 1 myotonic dystrophy (DM1) presented to the emergency department with dyspnea and palpitations.

Satellos said that it will be advancing its DMD small molecule to a Phase II trial, following the Phase I data.

An eight-member panel voted unanimously against wider use of Pfizer’s Talzenna in advanced prostate cancer. Elsewhere, U.K.

Sarepta Therapeutics (NASDAQ:SRPT) and its partner Roche (OTCQX:RHHBY) received a 'go ahead' from the regulatory body in U.K.

ALT, alanine aminotransferase; AST, aspartate aminotransferase; DMD, duchenne muscular dystrophy ... and Babinski's sign was not elicited bilaterally. Mild bilateral calf muscle hypertrophy with ...

New research led by the University of Portsmouth has revealed how Duchenne muscular dystrophy (DMD), best known for causing severe muscle degeneration, also profoundly affects the brain ...

Duchenne muscular dystrophy (DMD) is a rare neurological condition that causes severe muscle weakness and intellectual disability. DMD is an inherited (passed down) disorder. The condition is ...

The global Duchenne muscular dystrophy drugs market size reached USD 2.5 Billion in 2024. Looking forward, the market is projected to reach USD 5.9 Billion by 2033, exhibiting a growth rate (CAGR ...

Becker Muscular Dystrophy (BMD) is a genetic disorder first described by Peter Emil Becker in the 1950s. It is a milder variant of Duchenne Muscular Dystrophy ... such as progressive muscle wasting, ...

This year’s top stories on Duchenne muscular dystrophy (DMD) managed care included a novel imaging method for tracking disease progression, an FDA approval of the first nonsteroidal therapy ...

PTPN1/2 inhibition promotes muscle stem cell differentiation in Duchenne muscular dystrophy. Life Science Alliance , 2024; 8 (1): e202402831 DOI: 10.26508/lsa.202402831 Cite This Page : ...

The most common form, described by Duchenne ... with hypertrophy of the right ventricle but no changes of conduction or myocardial damage, which are usually observed in muscular dystrophy.