Imagine the gene that causes Huntington’s disease (HD) as a vast river. At its source is the CAG repeat - a genetic letter code that dictates how the river will flow. As the river moves downstream, it ...

Votoplam, the daily pill from PTC Therapeutics, has met its primary endpoint in the PIVOT-HD clinical trial - it can lower ...

Heart health has been linked to lower levels of NfL, a key biomarker of brain cell damage in Huntington’s disease. This ...

Huntington’s disease slows the cell’s protein factory, causing production line jams & toxicity. A faulty blueprint & missing factory assistant worsen errors. Targeting production slowdowns, not just ...

In plain language. Written by scientists. For the global HD community.