News

First Alert 4 on MSN13d
New gene therapy considered cure for Sickle Cell Disease being administered at St. Louis Children’s Hospital
A gene therapy recently approved by the FDA to treat patients with Sickle Cell Anemia is now being administered in St. Louis.
MIT Technology Review2d
This baby boy was treated with the first personalized gene-editing drug
The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely ...
Tribune Online on MSN1d
New medical advances offer fresh hope for sickle cell patients
Experts make case for early testing, prevention and care In this report, VINCENT KURAUN explores the groundbreaking ...
Gene editing cures child of rare disease in world first
Family overjoyed correction to DNA defect that causes metabolic disorder has given KJ Muldoon a new lease of life ...
Baby Is Healed With World’s First Personalized Gene-Editing Treatment
The technique used on a 9½-month-old boy with a rare condition has the potential to help people with thousands of other ...
Nasdaq4d
Editas Medicine Reports Promising In Vivo Gene Editing Results for Sickle Cell Disease and Beta Thalassemia at ASGCT Annual Meeting
Editas Medicine reports successful gene editing levels in stem cells, supporting potential treatment for sickle cell disease and beta thalassemia. Editas Medicine announced promising new data on ...
CHOP and Penn treated an infant with a rare disease by editing his genes
A Delaware County infant with a rare metabolic disease, CPS1 deficiency, was treated at CHOP with a custom CRISPR therapy.
Desperately ill baby healed with personalized gene therapy, doctors say
A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing ...
Sickle cell disease patients get disability certificates
Health camp certifies 35 sickle cell patients for disability benefits, emphasizing prevention, early detection, and community support.
Doctors successfully treated a baby with the first ever personalized gene-editing therapy
A team of doctors and scientists have successfully treated a rare genetic condition with the first-ever personalized ...
Fierce Healthcare13d
CMS will announce states participating in cell and gene therapy model—but health plans still have questions
In June, the Centers for Medicare & Medicaid Services (CMS) will name the participating states for the agency’s new Cell and ...
Child treated with gene editing therapy for the first time by a team of Philadelphia doctors
A team of doctors at the Children's Hospital of Philadelphia and Penn Medicine treated a baby with a gene editing technology ...