The biochemist introduced the first heel-prick tests for newborn babies in Spain, protecting infants from life-changing ...

SEMINOLE, Fla. (WFLA) — A Pinellas County mother is in a desperate fight to keep her 4-year-old son healthy. Gideon Bennett ...

A Pinellas County mother is in a desperate fight to keep her 4-year-old son healthy. Gideon Bennett has a rare genetic ...

A Seminole mom is fighting for her son’s health after a rare disorder left him dependent on a strict medical diet. But now, she’s facing an unexpected challenge: losing access to the ...

ACTIVATE-Kids is the First Study to Demonstrate Efficacy of an Oral Therapy for Children with PK Deficiency Who Are Not Regularly Transfused –– ...

Synthetic biology specialist Synlogic will start phase 3 testing of a drug for rare metabolic disorder phenylketonuria (PKU) next year, after reporting solid proof-of-concept data.

Research and Development (R&D) Expenses: R&D expenses were $82.8 million for the fourth quarter of 2024, compared to $77.5 million for the fourth quarter of 2023, and $301.3 million for the full year ...

BioMarin Pharmaceutical (NASDAQ:BMRN – Get Free Report) was upgraded by StockNews.com from a “buy” rating to a “strong-buy” rating in a research report issued on Tuesday. Other research analysts also ...

State of Alaska Department of Revenue cut its position in shares of BioMarin Pharmaceutical Inc. (NASDAQ:BMRN – Free Report) by 25.6% during the 4th quarter, according to the company in its most ...

An innovative organoid model mirrors the pancreas' complexity, generating all three key cell types to explore development and possible regeneration.