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Sarepta Therapeutics has followed through on its promise to file for accelerated approval of its gene therapy SRP-9001 for Duchenne muscular dystrophy ... measures of physical ability, although ...
For patients diagnosed with ALS and other neuromuscular conditions, specialized care is critical, but often out of reach.
Italfarmaco’s oral HDAC inhibitor givinostat has been approved in the US as a treatment for Duchenne muscular dystrophy (DMD ... also saw a slower decline in physical function over 18 months ...
A new business specializing in pediatric occupational, physical, and speech therapy will be holding its grand opening later ...
Columnist Betty Vertin acknowledges the mixed feelings of fear and pride as her youngest son with DMD begins with high school band.
Avidity has been given the go-ahead by the FDA to request accelerated approval of delpacibart braxlosiran—potentially the ...
The campaign to commemorate the work of the Muscular Dystrophy Association was created in partnership with agency Yes&.
We hypothesize that Duchenne muscular dystrophy and autism spectrum disorder/pervasive developmental disorder co-occur with a greater than random frequency. In this study, we set out to reject the ...
We identified a novel and significant association between Duchenne muscular dystrophy and autism spectrum disorder/pervasive developmental disorder. The eight cases with both diagnoses presented ...
Solve FSHD and Modalis Therapeutics Corp. have established a strategic collaboration to develop an innovative therapy for facioscapulohumeral muscular dystrophy (FSHD).
Therapy can feel like a big step, especially when you're unsure if a therapist will truly “get” you. My goal is to make this process meaningful, empowering, and real. Whether you're seeking ...
The aim of this study was to detect muscle imbalance on both sides of the backbone, and with muscle strength training, to correct this imbalance and, as a final result, to eliminate scoliosis of the ...
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