CINCINNATI (WKRC) - The annual "Cure SMA Walk-n-Roll" event kicked off Saturday morning at Xavier University, drawing ...

Hayden Yung finds ways to persevere with muscular dystrophy, but experts say targeted help is needed both for children and ...

Givinostat can slow the progression of Duchenne muscular dystrophy and is now available to some patients via an early access ...

From a missing sign turning up across the Irish sea, to cancelled festivals and teenagers locked in a play park - here are ...

Months after causing safety concerns that led the FDA to hit a related trial with a clinical hold, a phase 2 trial of ...

Advancements in gene therapy for Duchenne muscular dystrophy (DMD) have improved the outlook for some patients, but further ...

A rare and fatal form of muscular dystrophy has long posed a devastating diagnosis for children, primarily affecting boys.

Entrada has secured the authorisation within the EU Clinical Trial Regulation to begin the Phase I/II trial of ENTR-601-45.

In the Duchenne community they say time is muscle. So the clock is always ticking for the loved ones of those suffering with ...

Drug developer PepGen said on Wednesday it will discontinue development of its experimental therapy for Duchenne muscular dystrophy (DMD) after it failed to boost production of a protein in a ...

Living with a rare form of muscular dystrophy, and being honoured with having the youngest-ever seat on the board of trustees ...

PepGen ends Duchenne drug program after weak Phase 2 results, pivots to DM1 treatment showing early signs of splicing ...