We hypothesize that Duchenne muscular dystrophy and autism spectrum disorder/pervasive developmental disorder co-occur with a greater than random frequency. In this study, we set out to reject the ...

Local intramuscular administration of the antisense oligonucleotide PRO051 in patients with Duchenne's muscular dystrophy with relevant mutations was previously reported to induce the skipping of ...

Sarepta Therapeutics (NASDAQ:SRPT) and its partner Roche (OTCQX:RHHBY) received a 'go ahead' from the regulatory body in U.K.

The patient had DMD diagnosed when he was 5.5 years of age and had been treated over the course of 21 years with daily deflazacort (1.1 mg per kilogram per day). He lost the ability to ambulate ...

A 46-year-old woman with type 1 myotonic dystrophy (DM1) presented to the emergency department with dyspnea and palpitations.

Sarepta Therapeutics has followed through on its promise to file for accelerated approval of its gene therapy SRP-9001 for Duchenne muscular dystrophy (DMD), as it aims for a launch in the ...

Pfizer has axed trials of its domagrozumab antibody for Duchenne muscular dystrophy (DMD), after it failed against efficacy targets. Pfizer has been evaluating domagrozumab under the codename PF ...

An eight-member panel voted unanimously against wider use of Pfizer’s Talzenna in advanced prostate cancer. Elsewhere, U.K.

Satellos said that it will be advancing its DMD small molecule to a Phase II trial, following the Phase I data.

To truly optimise your time in the gym, however, it's worth needling in on the training protocols behind hypertrophy.We asked ...

A new report suggests combining the antimalarial drug with aminoglycosides could enhance the latter’s efficacy, which could also have important safety implications.

where she studies Norwegian patients with Duchenne muscular dystrophy who are under the age of 18. The author has completed the ICMJE form and declares the following conflict of interest: She has ...