Researchers have found a promising new method for gene therapy. They successfully restarted inactive genes by bringing them ...

CRSP bets on Casgevy to drive growth, but its extremely high price tag and slow rollout test investor patience in a crowded ...

India could take a leaf out of the Mahbubnagar district model, where 100 percent screening is done to keep a check on ...

Two main types of thalassemia exist, alpha and beta, depending on which part of the hemoglobin ... With new advances in biotechnology, gene editing has emerged as a promising alternative for treating ...

As the beta thalassemia landscape continues to evolve, hematologists are increasingly looking toward emerging therapies that are easier to prescribe, carry fewer logistical burdens than gene ...

KJ Muldoon, a 10-month-old baby, was diagnosed with the genetic disease carbamoyl-phosphate synthetase 1 deficiency after he ...

The clinical-stage biotech is developing gene-editing CRISPR technology. Editas has reported encouraging testing results in ...

Aiza was brought to Shanghai by her parents in January to undergo an experimental gene-editing therapy known as CS-101, a base-editing drug developed to treat severe beta-thalassemia.

While gene therapy has emerged as a promising alternative for treating beta-thalassemia, hematopoietic stem cell transplantation (HSCT) remains the only widely accessible curative option for this ...