Sickle Cell Disease Gene

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Gene, babies.Credit...Muldoon Family

Baby with rare disease given world-first personal CRISPR gene therapy

An infant with a severe genetic condition has shown signs of improvement after receiving a gene-editing treatment tailored to his specific mutation

MIT Technology Review · 1d

This baby boy was treated with the first personalized gene-editing drug

The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely rare genetic diseases.

The New York Times · 2d

Baby Is Healed With World’s First Personalized Gene-Editing Treatment

The technique used on a 9½-month-old boy with a rare condition has the potential to help people with thousands of other uncommon genetic diseases.

Tribune Online on MSN2h

New medical advances offer fresh hope for sickle cell patients

Experts make case for early testing, prevention and careIn this report, VINCENT KURAUN explores the groundbreaking strategies for managing sickle cell disease, with a particular focus on crisis ...

18h

Sickle cell disease patients get disability certificates

Health camp certifies 35 sickle cell patients for disability benefits, emphasizing prevention, early detection, and community support.

Nasdaq3d

Editas Medicine Reports Promising In Vivo Gene Editing Results for Sickle Cell Disease and Beta Thalassemia at ASGCT Annual Meeting

Editas Medicine reports successful gene editing levels in stem cells, supporting potential treatment for sickle cell disease and beta thalassemia. Editas Medicine announced promising new data ...

Fierce Healthcare12d

CMS will announce states participating in cell and gene therapy model—but health plans still have questions

In June, the Centers for Medicare & Medicaid Services (CMS) will name the participating states for the agency’s new Cell and ...

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