Avidity has been given the go-ahead by the FDA to request accelerated approval of delpacibart braxlosiran—potentially the ...

The Muscular Dystrophy Association trusts the decision ... that change how the muscle cells “read” the mutated gene, physical therapy or surgery to correct spinal curvature, Hesterlee said.“ ...

Duchenne muscular dystrophy (DMD ... Conventional drug treatments, such as steroids, combined with physical therapy remain the standard course of treatment despite merely delaying disease progression.

Columnist Betty Vertin acknowledges the mixed feelings of fear and pride as her youngest son with DMD begins with high school band.

While there is no cure for BMD, there are treatment options including occupational and physical therapy, foot and ankle braces, and wheelchairs. Children with Becker muscular dystrophy may start ...

Sarepta Therapeutics has followed through on its promise to file for accelerated approval of its gene therapy SRP-9001 for Duchenne muscular dystrophy ... measures of physical ability, although ...

Sixty-four cases of muscular dystrophy were diagnosed according ... One boy who was also receiving physical therapy with androstenolone had marked increases in strength and vital capacity.

Finally, their physical therapist recommended creatine kinase ... chief research officer of the Muscular Dystrophy Association. Elevidys works by delivering a shortened dystrophin gene, called ...

Satellos Bioscience Chief Scientific Officer discusses early-stage trials of the company's Duchenne muscular dystrophy drug, ...